Patisiran, an RNAi Therapeutic, for Hereditary Transthyretin Amyloidosis

Adams D., Gonzalez-Duarte A., O'Riordan W. D., Yang C. -., Ueda M., Kristen A. V., ...More

NEW ENGLAND JOURNAL OF MEDICINE, vol.379, no.1, pp.11-21, 2018 (SCI-Expanded, Scopus)

  • Publication Type: Article / Article
  • Volume: 379 Issue: 1
  • Publication Date: 2018
  • Doi Number: 10.1056/nejmoa1716153
  • Journal Name: NEW ENGLAND JOURNAL OF MEDICINE
  • Journal Indexes: Science Citation Index Expanded (SCI-EXPANDED), Scopus
  • Page Numbers: pp.11-21
  • Istanbul University Affiliated: Yes

Abstract

BACKGROUND