JOURNAL OF CLINICAL LIPIDOLOGY, vol.14, no.3, pp.361-372, 2020 (SCI-Expanded)
BACKGROUND: Homozygous familial hypercholesterolemia (HoFH) is a rare, life-threatening disease due to high serum low-density lipoprotein (LDL) cholesterol levels. LDL cholesterol-lowering interventions are fundamental for patients with HoFH.