ELIKIDS: Baseline characteristics from the eliglustat substrate reduction therapy trial in children with Gaucher disease type 1 or type 3


Giraldo P., GÖKÇAY G. F., Batsu I., Kissell J., Perichon M. G., Drelichman G. I.

19th Annual World Symposium, Florida, United States Of America, 21 - 26 February 2023, pp.47-48, (Summary Text) identifier

  • Publication Type: Conference Paper / Summary Text
  • Doi Number: 10.1016/j.ymgme.2022.107113
  • City: Florida
  • Country: United States Of America
  • Page Numbers: pp.47-48
  • Istanbul University Affiliated: Yes