ELIKIDS: baseline characteristics from the eliglustat substrate reduction therapy trial in children with Gaucher disease type 1 or type 3


Giraldo P., GÖKÇAY G. F., Batsu İ., Kissell J., Gaemers S. J., Li N., ...More

SSIEM Annual Symposium 2023, Jerusalem, Israel, 29 August 2023, vol.46, pp.307, (Summary Text)

  • Publication Type: Conference Paper / Summary Text
  • Volume: 46
  • City: Jerusalem
  • Country: Israel
  • Page Numbers: pp.307
  • Istanbul University Affiliated: Yes