MARALIXIBAT-TREATED PATIENTS WITH ALAGILLE SYNDROME DEMONSTRATE IMPROVED EVENT-FREE SURVIVAL IN A NATURAL HISTORY COMPARISON WITH PATIENTS FROM THE GALA DATABASE: APPLICATION OF REAL-WORLD EVIDENCE ANALYTICS.


Hansen B. E., Vandriel S. M., Vig P., Garner W., Loomes K. M., Piccoli D. A., ...More

NASPGHAN 2022 Annual Meeting, 12 - 15 October 2022, pp.211-213, (Summary Text)

  • Publication Type: Conference Paper / Summary Text
  • Page Numbers: pp.211-213
  • Istanbul University Affiliated: Yes